2019 Myotonic Annual Conference Agenda

Friday, September 13

• • 7:30 - 8:30

    Professional's Breakfast
    A light breakfast and coffee.

• • 8:30 - 9:45

    DM Biomarkers: Goals, What's Working & How They'll Be Used for Drug Development & Approval moderated by Charles Thornton, MD, University of Rochester.

    • Frank Bennett, PhD, Ionis Pharmaceuticals
    • Donovan Lott, PhD, PT, University of Florida
    • Peg Nopoulos, MD, University of Iowa
    • Jeffrey Statland, MD, University of Kansas
    • Matthew Tanner, MS, University of Rochester
    • Thurman Wheeler, MD, Massachusetts General Hospital
• • 9:45 - 10:00

    Coffee Break

• • 10:00 - 12:00

    Current Therapeutic Approaches moderated by Douglas Kerr, MD, PhD, MBA, Generation Bio.

    • Andrew Berglund, PhD, RNA Institute
    • Vincent Dion, PhD, Cardiff University School of Medicine
    • Matthew Disney, PhD, Scripps Research Institute
    • Steve Finkbeiner, MD, PhD, Gladstone Institutes
    • Darren Monckton, PhD, University of Glasgow
    • Christopher Pearson, PhD, Hospital for Sick Children
    • Romesh Subramanian, PhD, Dyne Therapeutics
    • Eugene Yeo, PhD, UCSD/Locana Bio
• • 12:00 - 12:30

    Lunch (Provided)

• • 13:00 - 13:30

    DM2 State of the Science: Current Research, Next Steps with Allison Formal, MBA.

• • 13:30 - 15:00

    Study & Trial Learnings to Date – Observations on Design, Endpoints & Patient Enrichment Strategies moderated by Kathie Bishop, PhD, Otonomy.

    • Guillaume Bassez, MD, PhD, Institut de Myologie
    • Chad Heatwole, MD, University of Rochester
    • Joseph Horrigan, MD, AMO Pharma
    • Laurence Mignon, PhD, Ionis Pharmaceuticals
    • Christopher Turner, MD, PhD, University College London
• • 15:00 - 15:15

    Break

• • 15:15 - 15:45

    PRMRP: Specifics of This International Research Funding Program & Strategies for Application with Jonathan Ryder, PhD, US Department of Defense

• • 15:45 - 17:30

    DM Animal Models: What We Have, What We Need & Why moderated by Thomas Cooper, MD, Baylor College of Medicine.

    • Laurent Bogdanik, PhD, The Jackson Labs
    • Genèvieve Gourdon, PhD, Institut de Myologie
    • Sharon Hesterlee, PhD, AskBio
    • Laura Ranum, PhD, University of Florida
    • Ashish Rao, MS, Baylor College of Medicine
    • Maurice Swanson, PhD, University of Florida
    • Charles Thornton, MD, University of Rochester
    • Eric Wang, PhD, University of Florida
    • Thurman Wheeler, MD, Massachusetts General Hospital
• • 17:30 - 19:30

    Welcome Reception
    Join community members and DM professionals at the opening reception. Hors d'oeuvres will be served and a cash bar will be available. Be sure to visit the research poster session that will occur during the reception.

  • 17:30 - 19:30

    Research Poster Sessions (During Welcome Reception)
    MDF research Fellows, industry professionals and academic researchers present their current research and answer questions via 1:1 discussions at their posters. Grab a beverage and circulate!